GA1: How natural history studies support the development of new treatments

Feb 25, 2026·
Curtis Coughlin II
Curtis Coughlin II
· 1 min read
photo from Dr. Steve Goodman
Abstract
This lecture will focus on natural history of GA1 post newborn screening and recent treatment advancements
Date
Feb 25, 2026
Event
Virtual webinar

Lecture overview

Dr. Coughlin provided a virtual talk on GA1. The foucsed of the talk was on natural history of GA1 including many unknown questions. We also disucssed several exciting therapeutic developments and highlighted the work of the CHARLIE Consoritum.

The Coughlin Lab is also leading a short natural history study with the aim to support clincial trials. If interested in more information either visit our recruitment website GA1 Study or contact our lab at Coughlin.Lab@cuanschutz.edu

GA1
Curtis Coughlin II
Authors
Curtis Coughlin II
Associate Professor
Translational researcher focused on rare diseases and bioethics